Clinical Trials In Rare Diseases & Clinical Data Management Innovation 2023 | Sponsors

Leading in Rare Disease Clinical Trials

Alexion Pharmaceuticals, Inc.

Clinical Trials For Rare Diseases: Challenges And Opportunities by Dr. Chris Missling, CEO Anavex LS

Precision Evolution Global

Barriers to Recruiting Patients for Rare Disease Clinical Trials

2nd Annual Clinical Trials in Rare Diseases | Hayley Mason

Arena International

Understanding the Challenges: Clinical Trials for Rare Diseases

Alexion Pharmaceuticals US

ASK THE EXPERT | Dr Richard Thompson, Findacure: Clinical trials for rare diseases

Informa Connect Life Sciences

Rare Diseases are Not Rare – A Training on Rare Disease Resources

Network of the National Library of Medicine [NNLM]

Clinical Trials In Rare Diseases 2023 | Karin Hoelzer

Arena International

Pharmacotherapy and Recent Advances in Neurodegenerative Disorders

FDA Draft Guidance: Rare Disease Clinical Trials

Rare Disease Research: Conducting Clinical Trials Where The Patients Are

Premier Research

Rare Disease Challenges in Each Step of the Drug Development Process

National Organization for Rare Disorders (NORD)

Clinical Trials and Rare Diseases

How Many Patients do you Need for a Rare Disease Clinical Trial?

Rare Disease Report

Clinical Trials In Rare Diseases 2023 | Michele Rhee

Arena International

2nd Annual Clinical Trials in Rare Diseases | Patrick Shores

Arena International

The Importance of Clinical Trials for Rare Disease Patients

The Balancing Act

Early Phase Trial designs in Rare diseases

EJP Rare Diseases

Efficient Clinical Trials for Rare Diseases, Thomas Jaki

LEADER 3D: Challenges, Strategies & Regulatory Considerations for Rare Disease Clinical Trial Design

U.S. Food and Drug Administration